Frontiers in Neurology (Oct 2021)
A Phase II Study to Evaluate the Safety and Efficacy of Prasinezumab in Early Parkinson's Disease (PASADENA): Rationale, Design, and Baseline Data
- Gennaro Pagano,
- Frank G. Boess,
- Kirsten I. Taylor,
- Kirsten I. Taylor,
- Benedicte Ricci,
- Brit Mollenhauer,
- Brit Mollenhauer,
- Werner Poewe,
- Anne Boulay,
- Judith Anzures-Cabrera,
- Annamarie Vogt,
- Maddalena Marchesi,
- Anke Post,
- Tania Nikolcheva,
- Gene G. Kinney,
- Wagner M. Zago,
- Daniel K. Ness,
- Hanno Svoboda,
- Markus Britschgi,
- Susanne Ostrowitzki,
- Tanya Simuni,
- Kenneth Marek,
- Martin Koller,
- Jeff Sevigny,
- Rachelle Doody,
- Paulo Fontoura,
- Daniel Umbricht,
- Azad Bonni,
- PASADENA Investigators,
- Prasinezumab Study Group,
- Claudia Altendorf,
- Chareyna Anandan,
- Giulia Andrews,
- Solène Ansquer,
- Raphaele Arrouasse,
- Sana Aslam,
- Jean-Philippe Azulay,
- Jeanette Baker,
- Ernest Balaguer Martinez,
- Shadi Barbu,
- Kara Bardram,
- Danny Bega,
- Helena Bejr-Kasem Marco,
- Isabelle Benatru,
- Eve Benchetrit,
- Felix Bernhard,
- Amir Besharat,
- Sagari Bette,
- Amelie Bichon,
- Andrew Billnitzer,
- Sophie Blondeau,
- Thomas Boraud,
- Freiderike Borngräber,
- James Boyd,
- Kathrin Brockmann,
- Matthew Brodsky,
- Ethan Brown,
- Christof Bruecke,
- Fabienne Calvas,
- Monica Canelo,
- Federico Carbone,
- Claire Carroll,
- Laura Casado Fernandez,
- Catherine Cassé-Perrot,
- Anna Castrioto,
- Helene Catala,
- Justine Chan,
- Samia Cheriet,
- Anthony Ciabarra,
- Joseph Classen,
- Juliana Coleman,
- Robert Coleman,
- Yaroslau Compta,
- Anne-Gaëlle Corbillé,
- Jean-Christophe Corvol,
- Mariana Cosgaya,
- Nabila Dahodwala,
- Philippe Damier,
- Elodie David,
- Thomas Davis,
- Marissa Dean,
- Berengere Debilly,
- Janell DeGiorgio,
- Andres Deik,
- Laure Delaby,
- Marie-Helene Delfini,
- Pascal Derkinderen,
- Philipp Derost,
- Maria de Toledo,
- Lisa Deuel,
- Ann Marie Diaz-Hernandez,
- Cameron Dietiker,
- Karina Dimenshteyn,
- Julio Dotor,
- Franck Durif,
- Jens Ebentheuer,
- Karla Maria Eggert,
- Sara Eichau Madueño,
- Claudia Eickhoff,
- Aaron Ellenbogen,
- Philipp Ellmerer,
- Ines Esparragosa Vazquez,
- Alexandre Eusebio,
- Siobhan Ewert,
- John Fang,
- Danielle Feigenbaum,
- Frederique Fluchere,
- Alexandra Foubert-Samier,
- Marie Fournier,
- Anne Fradet,
- Valerie Fraix,
- Samuel Frank,
- Franca Fries,
- Monique Galitzky,
- Marisol Gallardó Pérez,
- Jose Manuel García Moreno,
- Carmen Gasca,
- Thomas Gasser,
- Joyce Gibbons,
- Caroline Giordana,
- Alicia Gonzalez Martinez,
- Ira Goodman,
- Arantza Gorospe,
- Marie Goubeaud,
- David Grabli,
- Mangone Graziella,
- Stephan Grimaldi,
- Jeffrey Gross,
- Raquel Guimaraes-Costa,
- Andreas Hartmann,
- Christian Hartmann,
- Travis Hassell,
- Robert Hauser,
- Antonio Hernandez,
- Jorge Hernandez-Vara,
- Günter Höglinger,
- Christian Homedes,
- Andrea Horta-Barba,
- Jean-Luc Houeto,
- Julius Huebl,
- Jennifer Hui,
- Stuart Isaacson,
- Joseph Jankovic,
- Annette Janzen,
- Junior Jauregui,
- Jocelyne Jiao,
- Maria Jose Marti Domenech,
- Xavier Joseph,
- Srinath Kadimi,
- Pat Kaminski,
- Silja Kannenberg,
- Jan Kassubek,
- Maya Katz,
- Kevin Klos,
- Shannon Klos,
- Christopher Kobet,
- Jennifer Koebert,
- Patricia Krause,
- Andrea Kuehn,
- Jaime Kulisevsky Bojarsky,
- Rajeev Kumar,
- Martin Kunz,
- Lille Kurvits,
- Kimberly Kwei,
- Simon Laganiere,
- Brice Laurens,
- Johannes Levin,
- Oren Levy,
- Peter LeWitt,
- Gurutz Linazasoro Cristóbal,
- Irene Litvan,
- Karlo Lizarraga,
- Katherine Longardner,
- Rocio Lopez,
- Lydia Lopez Manzanares,
- Sara Lucas del Pozo,
- Maria Rosario Luquin Puido,
- Nijee Luthra,
- Kelly Lyons,
- Sylvia Maass,
- Gerrit Machetanz,
- Yolanda Macias,
- David Maltete,
- Jorge Uriel Manez Miro,
- Louise-Laure Mariani,
- Juan Marin,
- Kathrin Marini,
- Ana Marques,
- Gloria Marti,
- Maria Jose Marti Domenech,
- Saul Martinez,
- Wassilios Meissner,
- Sara Meoni,
- Brit Mollenhauer,
- Dunia Mon Martinez,
- Johnson Moon,
- Elena Moro,
- Peter Morrison,
- Christoph Muehlberg,
- Manpreet Multani,
- Christine Murphy,
- Anthony Nicholas,
- Rajesh Pahwa,
- Antonio Palasi,
- Heidi Pape,
- Neepa Patel,
- Prity Patel,
- Marina Peball,
- Elizabeth Peckham,
- Terry Peery,
- Rafael Perez,
- Jesus Perez,
- Alisa Petit,
- Elmar Pinkhardt,
- Werner Poewe,
- Elsa Pomies,
- Cecile Preterre,
- Joseph Quinn,
- Olivier Rascol,
- Philippe Remy,
- Irene Richard,
- Benjamin Roeben,
- Emily Ruether,
- Jost-Julian Rumpf,
- David Russell,
- Hayet Salhi,
- Daniela Samaniego-Toro,
- Alexandra Samier-Foubert,
- Antonio Sanchez,
- Emmanuelle Schmitt,
- Alfons Schnitzler,
- Oliver Schorr,
- Julie Schwartzbard,
- Kerstin Schweyer,
- Klaus Seppi,
- Victoria Sergo,
- Holly Shill,
- Andrew Siderowf,
- Tanya Simuni,
- Umberto Spampinato,
- Ashok Sriram,
- Natividad Stover,
- Caroline Tanner,
- Arjun Tarakad,
- Carolyn Taylor,
- Claire Thalamus,
- Thomas Toothaker,
- Nadege Van Blercom,
- Nora Vanegas-Arrogave,
- Lydia Vela,
- Sylvian Vergnet,
- Tiphaine Vidal,
- Jonathan Vöglein,
- Ryan Walsh,
- Cheryl Waters,
- Mirko Wegscheider,
- Endy Weidinger,
- Caroline Weill,
- Gregor Wenzel,
- Tatiana Witjas,
- Isabel Wurster,
- Brenton Wright,
- Milan Zimmermann,
- Rafael Zuzuarregui,
- Markus Abt,
- Atieh Bamdadian,
- Teresa Barata,
- Nicholas Barbet,
- Sara Belli,
- Frank Boess,
- Azad Bonni,
- Edilio Borroni,
- Anne Boulay,
- Markus Britschgi,
- Jerome Chague,
- Valerie Cosson,
- Christian Czech,
- Dennis Deptula,
- Cheikh Diack,
- Rachelle Doody,
- Juergen Dukart,
- Giulia D'Urso,
- Sebastian Dziadek,
- Hannah Eddleston,
- Chris Edgar,
- Laurent Essioux,
- Morgan Farell,
- Rebecca Finch,
- Paulo Fontoura,
- Waltraud Gruenbauer,
- Andrea Hahn,
- Stefan Holiga,
- Michael Honer,
- Shirin Jadidi,
- Kelly Johnson-Wood,
- Markus Keller,
- Timothy Kilchenmann,
- Martin Koller,
- Thomas Kremer,
- Thomas Kustermann,
- Claire Landsdall,
- Michael Lindemann,
- Florian Lipsmeier,
- Cecile Luzy,
- Marianne Manchester,
- Maddalena Marchesi,
- Ferenc Martenyi,
- Meret Martin-Facklam,
- Katerina Mironova,
- Annabelle Monnet,
- Emma Moore,
- Daniel K Ness,
- Markus Niggli,
- Tania Nikolcheva,
- Susanne Ostrowitzki,
- Gennaro Pagano,
- Benedicte Passmard,
- Agnes Poirier,
- Anke Post,
- Megana Prasad,
- Nathalie Pross,
- Tiffany Quock,
- Benedicte Ricci,
- Ellen Rose,
- Christoph Sarry,
- Christine Schubert,
- Dennis Selkoe,
- Jeff Sevigny,
- Kaycee Sink,
- Hannah Staunton,
- Tim Steven,
- Alexander Strasak,
- Hanno Svoboda,
- Kirsten Taylor,
- Radhika Tripuraneni,
- Dylan Trundell,
- Daniel Umbricht,
- Lynne Verselis,
- Annamarie Vogt,
- Ekaterina Volkova-Volkmar,
- Cornelia Weber,
- Silke Weber,
- Wagner Zago
Affiliations
- Gennaro Pagano
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Frank G. Boess
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Kirsten I. Taylor
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Kirsten I. Taylor
- Faculty of Psychology, University of Basel, Basel, Switzerland
- Benedicte Ricci
- Roche Pharma Research and Early Development (pRED), Pharmaceutical Sciences, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Brit Mollenhauer
- Paracelsus-Elena-Klinik, Kassel, Germany
- Brit Mollenhauer
- Department of Neurology, University Medical Center Göttingen, Göttingen, Germany
- Werner Poewe
- Department of Neurology, Innsbruck Medical University, Innsbruck, Austria
- Anne Boulay
- Idorisa Pharmaceuticals Ltd., Allschwil, Switzerland
- Judith Anzures-Cabrera
- Roche Products Ltd., Welwyn Garden City, United Kingdom
- Annamarie Vogt
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Maddalena Marchesi
- Roche Pharma Research and Early Development (pRED), Pharmaceutical Sciences, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Anke Post
- Feetme SAS, Paris, France
- Tania Nikolcheva
- 0F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Gene G. Kinney
- 1Prothena Biosciences Inc., South San Francisco, CA, United States
- Wagner M. Zago
- 1Prothena Biosciences Inc., South San Francisco, CA, United States
- Daniel K. Ness
- 1Prothena Biosciences Inc., South San Francisco, CA, United States
- Hanno Svoboda
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Markus Britschgi
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Susanne Ostrowitzki
- 0F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Tanya Simuni
- 2Department of Neurology, Northwestern University Feinberg School of Medicine, Chicago, IL, United States
- Kenneth Marek
- 3Institute for Neurodegenerative Disorders, New Haven, CT, United States
- Martin Koller
- 1Prothena Biosciences Inc., South San Francisco, CA, United States
- Jeff Sevigny
- 4Prevail Therapeutics, New York, NY, United States
- Rachelle Doody
- 0F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Paulo Fontoura
- 0F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Daniel Umbricht
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- Azad Bonni
- Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center, F. Hoffmann-La Roche Ltd., Basel, Switzerland
- PASADENA Investigators
- Prasinezumab Study Group
- Claudia Altendorf
- Chareyna Anandan
- Giulia Andrews
- Solène Ansquer
- Raphaele Arrouasse
- Sana Aslam
- Jean-Philippe Azulay
- Jeanette Baker
- Ernest Balaguer Martinez
- Shadi Barbu
- Kara Bardram
- Danny Bega
- Helena Bejr-Kasem Marco
- Isabelle Benatru
- Eve Benchetrit
- Felix Bernhard
- Amir Besharat
- Sagari Bette
- Amelie Bichon
- Andrew Billnitzer
- Sophie Blondeau
- Thomas Boraud
- Freiderike Borngräber
- James Boyd
- Kathrin Brockmann
- Matthew Brodsky
- Ethan Brown
- Christof Bruecke
- Fabienne Calvas
- Monica Canelo
- Federico Carbone
- Claire Carroll
- Laura Casado Fernandez
- Catherine Cassé-Perrot
- Anna Castrioto
- Helene Catala
- Justine Chan
- Samia Cheriet
- Anthony Ciabarra
- Joseph Classen
- Juliana Coleman
- Robert Coleman
- Yaroslau Compta
- Anne-Gaëlle Corbillé
- Jean-Christophe Corvol
- Mariana Cosgaya
- Nabila Dahodwala
- Philippe Damier
- Elodie David
- Thomas Davis
- Marissa Dean
- Berengere Debilly
- Janell DeGiorgio
- Andres Deik
- Laure Delaby
- Marie-Helene Delfini
- Pascal Derkinderen
- Philipp Derost
- Maria de Toledo
- Lisa Deuel
- Ann Marie Diaz-Hernandez
- Cameron Dietiker
- Karina Dimenshteyn
- Julio Dotor
- Franck Durif
- Jens Ebentheuer
- Karla Maria Eggert
- Sara Eichau Madueño
- Claudia Eickhoff
- Aaron Ellenbogen
- Philipp Ellmerer
- Ines Esparragosa Vazquez
- Alexandre Eusebio
- Siobhan Ewert
- John Fang
- Danielle Feigenbaum
- Frederique Fluchere
- Alexandra Foubert-Samier
- Marie Fournier
- Anne Fradet
- Valerie Fraix
- Samuel Frank
- Franca Fries
- Monique Galitzky
- Marisol Gallardó Pérez
- Jose Manuel García Moreno
- Carmen Gasca
- Thomas Gasser
- Joyce Gibbons
- Caroline Giordana
- Alicia Gonzalez Martinez
- Ira Goodman
- Arantza Gorospe
- Marie Goubeaud
- David Grabli
- Mangone Graziella
- Stephan Grimaldi
- Jeffrey Gross
- Raquel Guimaraes-Costa
- Andreas Hartmann
- Christian Hartmann
- Travis Hassell
- Robert Hauser
- Antonio Hernandez
- Jorge Hernandez-Vara
- Günter Höglinger
- Christian Homedes
- Andrea Horta-Barba
- Jean-Luc Houeto
- Julius Huebl
- Jennifer Hui
- Stuart Isaacson
- Joseph Jankovic
- Annette Janzen
- Junior Jauregui
- Jocelyne Jiao
- Maria Jose Marti Domenech
- Xavier Joseph
- Srinath Kadimi
- Pat Kaminski
- Silja Kannenberg
- Jan Kassubek
- Maya Katz
- Kevin Klos
- Shannon Klos
- Christopher Kobet
- Jennifer Koebert
- Patricia Krause
- Andrea Kuehn
- Jaime Kulisevsky Bojarsky
- Rajeev Kumar
- Martin Kunz
- Lille Kurvits
- Kimberly Kwei
- Simon Laganiere
- Brice Laurens
- Johannes Levin
- Oren Levy
- Peter LeWitt
- Gurutz Linazasoro Cristóbal
- Irene Litvan
- Karlo Lizarraga
- Katherine Longardner
- Rocio Lopez
- Lydia Lopez Manzanares
- Sara Lucas del Pozo
- Maria Rosario Luquin Puido
- Nijee Luthra
- Kelly Lyons
- Sylvia Maass
- Gerrit Machetanz
- Yolanda Macias
- David Maltete
- Jorge Uriel Manez Miro
- Louise-Laure Mariani
- Juan Marin
- Kathrin Marini
- Ana Marques
- Gloria Marti
- Maria Jose Marti Domenech
- Saul Martinez
- Wassilios Meissner
- Sara Meoni
- Brit Mollenhauer
- Dunia Mon Martinez
- Johnson Moon
- Elena Moro
- Peter Morrison
- Christoph Muehlberg
- Manpreet Multani
- Christine Murphy
- Anthony Nicholas
- Rajesh Pahwa
- Antonio Palasi
- Heidi Pape
- Neepa Patel
- Prity Patel
- Marina Peball
- Elizabeth Peckham
- Terry Peery
- Rafael Perez
- Jesus Perez
- Alisa Petit
- Elmar Pinkhardt
- Werner Poewe
- Elsa Pomies
- Cecile Preterre
- Joseph Quinn
- Olivier Rascol
- Philippe Remy
- Irene Richard
- Benjamin Roeben
- Emily Ruether
- Jost-Julian Rumpf
- David Russell
- Hayet Salhi
- Daniela Samaniego-Toro
- Alexandra Samier-Foubert
- Antonio Sanchez
- Emmanuelle Schmitt
- Alfons Schnitzler
- Oliver Schorr
- Julie Schwartzbard
- Kerstin Schweyer
- Klaus Seppi
- Victoria Sergo
- Holly Shill
- Andrew Siderowf
- Tanya Simuni
- Umberto Spampinato
- Ashok Sriram
- Natividad Stover
- Caroline Tanner
- Arjun Tarakad
- Carolyn Taylor
- Claire Thalamus
- Thomas Toothaker
- Nadege Van Blercom
- Nora Vanegas-Arrogave
- Lydia Vela
- Sylvian Vergnet
- Tiphaine Vidal
- Jonathan Vöglein
- Ryan Walsh
- Cheryl Waters
- Mirko Wegscheider
- Endy Weidinger
- Caroline Weill
- Gregor Wenzel
- Tatiana Witjas
- Isabel Wurster
- Brenton Wright
- Milan Zimmermann
- Rafael Zuzuarregui
- Markus Abt
- Atieh Bamdadian
- Teresa Barata
- Nicholas Barbet
- Sara Belli
- Frank Boess
- Azad Bonni
- Edilio Borroni
- Anne Boulay
- Markus Britschgi
- Jerome Chague
- Valerie Cosson
- Christian Czech
- Dennis Deptula
- Cheikh Diack
- Rachelle Doody
- Juergen Dukart
- Giulia D'Urso
- Sebastian Dziadek
- Hannah Eddleston
- Chris Edgar
- Laurent Essioux
- Morgan Farell
- Rebecca Finch
- Paulo Fontoura
- Waltraud Gruenbauer
- Andrea Hahn
- Stefan Holiga
- Michael Honer
- Shirin Jadidi
- Kelly Johnson-Wood
- Markus Keller
- Timothy Kilchenmann
- Martin Koller
- Thomas Kremer
- Thomas Kustermann
- Claire Landsdall
- Michael Lindemann
- Florian Lipsmeier
- Cecile Luzy
- Marianne Manchester
- Maddalena Marchesi
- Ferenc Martenyi
- Meret Martin-Facklam
- Katerina Mironova
- Annabelle Monnet
- Emma Moore
- Daniel K Ness
- Markus Niggli
- Tania Nikolcheva
- Susanne Ostrowitzki
- Gennaro Pagano
- Benedicte Passmard
- Agnes Poirier
- Anke Post
- Megana Prasad
- Nathalie Pross
- Tiffany Quock
- Benedicte Ricci
- Ellen Rose
- Christoph Sarry
- Christine Schubert
- Dennis Selkoe
- Jeff Sevigny
- Kaycee Sink
- Hannah Staunton
- Tim Steven
- Alexander Strasak
- Hanno Svoboda
- Kirsten Taylor
- Radhika Tripuraneni
- Dylan Trundell
- Daniel Umbricht
- Lynne Verselis
- Annamarie Vogt
- Ekaterina Volkova-Volkmar
- Cornelia Weber
- Silke Weber
- Wagner Zago
- DOI
- https://doi.org/10.3389/fneur.2021.705407
- Journal volume & issue
-
Vol. 12
Abstract
Background: Currently available treatments for Parkinson's disease (PD) do not slow clinical progression nor target alpha-synuclein, a key protein associated with the disease.Objective: The study objective was to evaluate the efficacy and safety of prasinezumab, a humanized monoclonal antibody that binds aggregated alpha-synuclein, in individuals with early PD.Methods: The PASADENA study is a multicenter, randomized, double-blind, placebo-controlled treatment study. Individuals with early PD, recruited across the US and Europe, received monthly intravenous doses of prasinezumab (1,500 or 4,500 mg) or placebo for a 52-week period (Part 1), followed by a 52-week extension (Part 2) in which all participants received active treatment. Key inclusion criteria were: aged 40–80 years; Hoehn & Yahr (H&Y) Stage I or II; time from diagnosis ≤2 years; having bradykinesia plus one other cardinal sign of PD (e.g., resting tremor, rigidity); DAT-SPECT imaging consistent with PD; and either treatment naïve or on a stable monoamine oxidase B (MAO-B) inhibitor dose. Study design assumptions for sample size and study duration were built using a patient cohort from the Parkinson's Progression Marker Initiative (PPMI). In this report, baseline characteristics are compared between the treatment-naïve and MAO-B inhibitor-treated PASADENA cohorts and between the PASADENA and PPMI populations.Results: Of the 443 patients screened, 316 were enrolled into the PASADENA study between June 2017 and November 2018, with an average age of 59.9 years and 67.4% being male. Mean time from diagnosis at baseline was 10.11 months, with 75.3% in H&Y Stage II. Baseline motor and non-motor symptoms (assessed using Movement Disorder Society—Unified Parkinson's Disease Rating Scale [MDS-UPDRS]) were similar in severity between the MAO-B inhibitor-treated and treatment-naïve PASADENA cohorts (MDS-UPDRS sum of Parts I + II + III [standard deviation (SD)]; 30.21 [11.96], 32.10 [13.20], respectively). The overall PASADENA population (63.6% treatment naïve and 36.4% on MAO-B inhibitor) showed a similar severity in MDS-UPDRS scores (e.g., MDS-UPDRS sum of Parts I + II + III [SD]; 31.41 [12.78], 32.63 [13.04], respectively) to the PPMI cohort (all treatment naïve).Conclusions: The PASADENA study population is suitable to investigate the potential of prasinezumab to slow disease progression in individuals with early PD.Trial Registration: NCT03100149.
Keywords
- Parkinson's disease
- alpha-synuclein (α-syn)
- prasinezumab
- monoclonal antibodies
- disease progression
- MDS-UPDRS = Movement Disorder Society—Unified Parkinson's Disease Rating Scale