Safety and improved efficacy signals following gene therapy in childhood blindness caused by GUCY2D mutations

• Samuel G. Jacobson,
• Artur V. Cideciyan,
• Allen C. Ho,
• Igor V. Peshenko,
• Alexandra V. Garafalo,
• Alejandro J. Roman,
• Alexander Sumaroka,
• Vivian Wu,
• Arun K. Krishnan,
• Rebecca Sheplock,
• Sanford L. Boye,
• Alexander M. Dizhoor,
• Shannon E. Boye

Affiliations

Samuel G. Jacobson

Corresponding author

Artur V. Cideciyan

Allen C. Ho

Igor V. Peshenko

Alexandra V. Garafalo

Alejandro J. Roman

Alexander Sumaroka

Vivian Wu

Arun K. Krishnan

Rebecca Sheplock

Sanford L. Boye

Alexander M. Dizhoor

Shannon E. Boye