Frontiers in Immunology (Jul 2023)
Five-year follow-up of a phase I trial of donor-derived modified immune cell infusion in kidney transplantation
- Matthias Schaier,
- Matthias Schaier,
- Christian Morath,
- Christian Morath,
- Christian Morath,
- Lei Wang,
- Lei Wang,
- Christian Kleist,
- Christian Kleist,
- Gerhard Opelz,
- Thuong Hien Tran,
- Sabine Scherer,
- Lien Pham,
- Naruemol Ekpoom,
- Caner Süsal,
- Caner Süsal,
- Gerald Ponath,
- Gerald Ponath,
- Florian Kälble,
- Claudius Speer,
- Louise Benning,
- Christian Nusshag,
- Christoph F. Mahler,
- Luiza Pego da Silva,
- Claudia Sommerer,
- Claudia Sommerer,
- Angela Hückelhoven-Krauss,
- David Czock,
- Arianeb Mehrabi,
- Constantin Schwab,
- Rüdiger Waldherr,
- Paul Schnitzler,
- Uta Merle,
- Vedat Schwenger,
- Markus Krautter,
- Stephan Kemmner,
- Michael Fischereder,
- Manfred Stangl,
- Ingeborg A. Hauser,
- Anna-Isabelle Kälsch,
- Bernhard K. Krämer,
- Georg A. Böhmig,
- Carsten Müller-Tidow,
- Jochen Reiser,
- Martin Zeier,
- Michael Schmitt,
- Peter Terness,
- Anita Schmitt,
- Anita Schmitt,
- Volker Daniel
Affiliations
- Matthias Schaier
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Matthias Schaier
- TolerogenixX GmbH, Heidelberg, ;Germany
- Christian Morath
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Christian Morath
- TolerogenixX GmbH, Heidelberg, ;Germany
- Christian Morath
- German Center for Infection Research, German Center for Infection Research (DZIF), Thematic Translational Unit (TTU)-Infections of the Immunocompromised Host (IICH), Partner Site Heidelberg, Heidelberg, ;Germany
- Lei Wang
- TolerogenixX GmbH, Heidelberg, ;Germany
- Lei Wang
- Department of Hematology, Oncology and Rheumatology, Heidelberg University Hospital, Heidelberg, ;Germany
- Christian Kleist
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Christian Kleist
- Department of Nuclear Medicine, Heidelberg University Hospital, Heidelberg, ;Germany
- Gerhard Opelz
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Thuong Hien Tran
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Sabine Scherer
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Lien Pham
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Naruemol Ekpoom
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Caner Süsal
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Caner Süsal
- Transplant Immunology Research Center of Excellence, Koç University, Istanbul, ;Türkiye
- Gerald Ponath
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Gerald Ponath
- TolerogenixX GmbH, Heidelberg, ;Germany
- Florian Kälble
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Claudius Speer
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Louise Benning
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Christian Nusshag
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Christoph F. Mahler
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Luiza Pego da Silva
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Claudia Sommerer
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Claudia Sommerer
- German Center for Infection Research, German Center for Infection Research (DZIF), Thematic Translational Unit (TTU)-Infections of the Immunocompromised Host (IICH), Partner Site Heidelberg, Heidelberg, ;Germany
- Angela Hückelhoven-Krauss
- Department of Hematology, Oncology and Rheumatology, Heidelberg University Hospital, Heidelberg, ;Germany
- David Czock
- Department of Clinical Pharmacology and Pharmacoepidemiology, Heidelberg University Hospital, Heidelberg, ;Germany
- Arianeb Mehrabi
- Department of General, Visceral and Transplantation Surgery, Heidelberg University Hospital, Heidelberg, ;Germany
- Constantin Schwab
- 0Institute of Pathology, Heidelberg University Hospital, Heidelberg, ;Germany
- Rüdiger Waldherr
- 0Institute of Pathology, Heidelberg University Hospital, Heidelberg, ;Germany
- Paul Schnitzler
- 1Center for Infectious Diseases, Virology, Heidelberg University Hospital, Heidelberg, ;Germany
- Uta Merle
- 2Department of Gastroenterology, Heidelberg University Hospital, Heidelberg, ;Germany
- Vedat Schwenger
- 3Department of Nephrology, Klinikum der Landeshauptstadt Stuttgart, Stuttgart, ;Germany
- Markus Krautter
- 3Department of Nephrology, Klinikum der Landeshauptstadt Stuttgart, Stuttgart, ;Germany
- Stephan Kemmner
- 4Transplant Center, University Hospital Munich, Ludwig-Maximilians University (LMU), Munich, ;Germany
- Michael Fischereder
- 5Division of Nephrology, Department of Internal Medicine IV, University Hospital Munich, Ludwig-Maximilians-Universität München (LMU), Munich, ;Germany
- Manfred Stangl
- 6Department of General, Visceral, and Transplant Surgery, University Hospital Munich, Ludwig-Maximilians-Universität München (LMU), Munich, ;Germany
- Ingeborg A. Hauser
- 7Medical Clinic III, Department of Nephrology, University Hospital Frankfurt, Goethe University, Frankfurt am Main, ;Germany
- Anna-Isabelle Kälsch
- 8Fifth Department of Medicine (Nephrology/Endocrinology/Rheumatology/Pneumology), University Medical Centre Mannheim, University of Heidelberg, Mannheim, ;Germany
- Bernhard K. Krämer
- 8Fifth Department of Medicine (Nephrology/Endocrinology/Rheumatology/Pneumology), University Medical Centre Mannheim, University of Heidelberg, Mannheim, ;Germany
- Georg A. Böhmig
- 9Division of Nephrology and Dialysis, Department of Medicine III, Medical University of Vienna, Vienna, ;Austria
- Carsten Müller-Tidow
- Department of Hematology, Oncology and Rheumatology, Heidelberg University Hospital, Heidelberg, ;Germany
- Jochen Reiser
- 0Department of Medicine, Rush University, Chicago, IL, ;United States
- Martin Zeier
- Department of Nephrology, Heidelberg University Hospital, Heidelberg, ;Germany
- Michael Schmitt
- Department of Hematology, Oncology and Rheumatology, Heidelberg University Hospital, Heidelberg, ;Germany
- Peter Terness
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- Anita Schmitt
- TolerogenixX GmbH, Heidelberg, ;Germany
- Anita Schmitt
- Department of Hematology, Oncology and Rheumatology, Heidelberg University Hospital, Heidelberg, ;Germany
- Volker Daniel
- Institute of Immunology, Heidelberg University Hospital, Heidelberg, ;Germany
- DOI
- https://doi.org/10.3389/fimmu.2023.1089664
- Journal volume & issue
-
Vol. 14
Abstract
BackgroundThe administration of modified immune cells (MIC) before kidney transplantation led to specific immunosuppression against the allogeneic donor and a significant increase in regulatory B lymphocytes. We wondered how this approach affected the continued clinical course of these patients.MethodsTen patients from a phase I clinical trial who had received MIC infusions prior to kidney transplantation were retrospectively compared to 15 matched standard-risk recipients. Follow-up was until year five after surgery.ResultsThe 10 MIC patients had an excellent clinical course with stable kidney graft function, no donor-specific human leukocyte antigen antibodies (DSA) or acute rejections, and no opportunistic infections. In comparison, a retrospectively matched control group receiving standard immunosuppressive therapy had a higher frequency of DSA (log rank P = 0.046) and more opportunistic infections (log rank P = 0.033). Importantly, MIC patients, and in particular the four patients who had received the highest cell number 7 days before surgery and received low immunosuppression during follow-up, continued to show a lack of anti-donor T lymphocyte reactivity in vitro and high CD19+CD24hiCD38hi transitional and CD19+CD24hiCD27+ memory B lymphocytes until year five after surgery.ConclusionsMIC infusions together with reduced conventional immunosuppression were associated with good graft function during five years of follow-up, no de novo DSA development and no opportunistic infections. In the future, MIC infusions might contribute to graft protection while reducing the side effects of immunosuppressive therapy. However, this approach needs further validation in direct comparison with prospective controls.Trial registrationhttps://clinicaltrials.gov/, identifier NCT02560220 (for the TOL-1 Study). EudraCT Number: 2014-002086-30.
Keywords
- transplantation - kidney
- tolerance
- cell therapy
- regulatory B (Breg) cells
- phase I (drug development)