P1520: AN ACTIVIN RECEPTOR IIB LIGAND TRAP, IN COMBINATION WITH TMPRSS6 INDUCED IRON-RESTRICTION, IS A SUPERIOR TREATMENT FOR CORRECTING Β-THALASSEMIA IN MICE

• A. Guerra,
• P. Demsko,
• S. Sinha,
• P. McVeigh,
• C. Castruccio Castracani,
• L. Breda,
• C. Casu,
• S. Guo,
• S. Rivella

Affiliations

A. Guerra

1 Pediatrics, Children’s Hospital of Philadelphia

P. Demsko

2 Pediatrics, University of Pennsylvania, Perelman School of Medicine, Philadelphia

S. Sinha

1 Pediatrics, Children’s Hospital of Philadelphia

P. McVeigh

1 Pediatrics, Children’s Hospital of Philadelphia

C. Castruccio Castracani

1 Pediatrics, Children’s Hospital of Philadelphia

L. Breda

1 Pediatrics, Children’s Hospital of Philadelphia

C. Casu

1 Pediatrics, Children’s Hospital of Philadelphia

S. Guo

3 Pediatrics, Ionis Pharmaceuticals, Inc., Carlsbad, United States of America

S. Rivella

1 Pediatrics, Children’s Hospital of Philadelphia