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HemaSphere
(Jan 2022)
S101: COMBINATION OF A LUSPATERCEPT-LIKE DRUG (RAP-GRL) AND TMPRSS6-ASO IS SUPERIOR TO EITHER DRUG ALONE FOR CORRECTING β-THALASSEMIA
A. Guerra,
P. Demsko,
S. Sinha,
P. McVeigh,
C. Castruccio Castracani,
L. Breda,
C. Casu,
S. Rivella
Affiliations
A. Guerra
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
P. Demsko
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
S. Sinha
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
P. McVeigh
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
C. Castruccio Castracani
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
L. Breda
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
C. Casu
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
S. Rivella
Children’s Hospital Of Philadelphia, Philadelphia, UNITED STATES
DOI
https://doi.org/10.1097/HS9.0000000000000684
Journal volume & issue
Vol. 6
pp. 1 – 1
Abstract
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No abstracts available.
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